rare
Age-based approvals for rare diseases can be devastating
For most of my life, my family advocated for therapies to help my twin brother. Although the recent approval of a new drug should give us reason to celebrate, there is still work to be done. My twin brother is 28 years old and suffers from severe Hunter syndrome, also known as mucopolysaccharidosis (MPS) type […]
9 mins read
Roche suffers another blow as Indian Supreme Court allows sale of generics of its expensive rare disease drug
In a case billed as profiteering against patients, India’s Supreme Court rejected a petition in which Roche sought to stop a generic drugmaker from selling a cheaper version of an expensive rare disease drug. The move comes after a lower court earlier this month upheld a ruling that it would be in the public interest […]
1 min read